Study of gene therapy by “Exon skipping” for intronic mutations in pre-clinical phase
Study of gene therapy by "exon skipping" for intronic mutations in the pre-clinical phase Project…
Development of Selective Silencing Mutation as a Therapy for the Collagen VI Related Dystrophies.
Development of Selective Mutation Silencing as a Therapy for the Collagen VI Related Dystrophies. Project…
”Natural History, diagnosis and treatment of collagen VI-related muscular dystrophies”
"Natural History, diagnosis and treatment of collagen VI-related muscular dystrophies" Project description The project includes:…